ORPHAN DRUGS: REVIEW ARTICLE

Year 2023, Volume: 40 Issue: 4, 792 - 794, 03.01.2024

Hilal Aksoy

Abstract

Drugs which have limited access and are used treat rare diseases, are called "orphan drugs".
The reason why these drugs are called "orphan" is that the pharmaceutical industry has little interest in developing and marketing these drugs which are used only for a low number of patient groups This is because pharmaceutical companies cannot compensate the very high cost of developing these drugs. In this review article it is aimed to give information about orphan drugs, policies about these drugs and difficulties to reach them.

Keywords

orphan drugs, rare diseases, pharmaceutic, marketing

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